Diseases Treated.
Full List of FDA-Approved Cord Blood Treatments

LEUKEMIAS, LYMPHOMAS and BONE MARROW CANCERS: Cancers of the blood cells that make up the immune system.
- Acute Lymphoblastic/Lympocytic Leukemia (ALL)
 - Acute Myelogenous Leukemia (AML)
 - Acute Biphenotypic Leukemia
 - Acute Undifferentiated Leukemia
 - Adult T-cell Leukemia/Lymphoma
 - Chronic Lymphocytic Leukemia (CLL)
 - Chronic Myelogenous Leukemia (CML)
 - Chronic Myelomonocytic Leukemia (CMML)
 - Hodgkin’s Lymphoma
 - Juvenile Chronic Myelogenous Leukemia (JCML)
 - Juvenile Myelomonocytic Leukemia (JMML)
 - Multiple Myeloma
 - Myelodysplastic Syndrome
 - Myeloid/Natural Killer (NK) Cell Precursor Acute Leukemia
 - Non-Hodgkin’s Lymphoma
 - Plasma Cell Leukemia
 - Prolymphocytic Leukemia
 - Refractory Anemia (RA)
 - Refractory Anemia with Ringed Sideroblasts (RARS)
 - Refractory Anemia with Excess Blasts (RAEB)
 - Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
 - Waldenstrom’s Macroglobulinemia
 
SOLID TUMORS: Cancers of cells from organs of the body.
- Ewing Sarcoma
 - Medulloblastoma
 - Nephroblastoma (Wilms Tumor)
 - Neuroblastoma
 - Retinoblastoma
 - Rhabdomyosarcoma
 - Thymoma (Thymic Carcinoma)
 
ANEMIAS: Diseases causing too few blood cells to be made.
- Aplastic Anemia (Severe)
 - Congenital Cytopenia
 - Congenital Dyserythropoietic Anemia
 - Fanconi Anemia
 - Paroxysmal Nocturnal Hemoglobinuria (PNH)
 
INHERITED RED CELL ABNORMALITIES: Genetic diseases resulting in red blood cells that do not work correctly.
- Beta Thalassemia Major (also known as Cooley’s Anemia)
 - Blackfan-Diamond Anemia
 - Pure Red Cell Aplasia
 - Sickle Cell Disease
 
INHERITED PLATELET ABNORMALITIES: Genetic diseases resulting in platelets that are not able to correctly form clots.
Button- Amegakaryocytosis / Congenital Thrombocytopenia
 - Glanzmann Thrombasthenia
 
IMMUNE SYSTEM DISORDERS: Genetic or acquired diseases which result in white blood cells that are not able to fight off infections.
Button- Acute Myelofibrosis
 - Agnogenic Myeloid Metaplasia (Myelofibrosis)
 - Ataxia-Telangiectasia
 - Bare Lymphocyte Syndrome
 - Cartilage-Hair Hypoplasia
 - Chediak-Higashi Syndrome
 - Chronic Active Epstein Barr Virus
 - Chronic Granulomatous Disease
 - Common Variable Immunodeficiency
 - Congenital Neutropenia
 - DiGeorge Syndrome
 - Dyskeratosis Congenita
 - Essential Thrombocythemia
 - Evans Syndrome
 - Gunther’s Disease (Congenital Erythropoietic Porphyria)
 - IKK Gamma Deficiency (NEMO Deficiency)
 - Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-linked (IPEX) Syndrome
 - Hemophagocytic Lymphohistiocytosis (HLH)
 - Hermansky-Pudlak Syndrome
 - Kostmann Syndrome
 - Langerhans Cell Histiocytosis (Histiocytosis X)
 - Leukocyte Adhesion Deficiency
 - Lymphoproliferative Disorders (LPD)
 - Lymphoproliferative Disorder, X-linked (also known as Epstein-Barr Virus Susceptibility)
 - Myelokathexis
 - Myeloproliferative Disorders
 - Neutrophil Actin Deficiency
 - Omenn Syndrome (SCID)
 - Pearson’s Syndrome
 - Polycythemia Vera
 - Reticular Dysgenesis (SCID)
 - SCID with Adenosine Deaminase Deficiency (ADA-SCID)
 - SCID with absence of T & B Cells
 - SCID with absence of T cells, Normal B Cells
 - SCID with Purine Nucleoside Phosphorylase Deficiency
 - SCID which is X-linked
 - Shwachman-Diamond Syndrome
 - Systemic Amyloidosis
 - Systemic Mastocytosis
 - Thymic dysplasia
 - Wiskott-Aldrich Syndrome
 - X-linked Agammaglobulinemia
 - X-linked Hyper-IgM Syndrome
 - X-linked Lymphoproliferative Disorder
 
INHERITED METABOLIC DISORDERS: Genetic diseases that prevent the body from correctly processing normal substances in the body or diet.
Button- Adrenoleukodystrophy (ALD)/Adrenomyeloneuropathy (AMN)
 - Fucosidosis
 - Gaucher Disease
 - Hunter’s Syndrome (MPS-II)
 - Hurler’s Syndrome (MPS-IH)
 - Krabbe Disease (Globoid Cell Leukodystrophy)
 - Lesch-Nyhan Syndrom
 - Mannosidosis
 - Maroteaux-Lamy Syndrome (MPS-VI)
 - Metachromatic Leukodystrophy
 - Morquio Syndrome (MPS-IV)
 - Mucolipidosis II (I-cell Disease)
 - Mucopolysaccharidoses (MPS)
 - Niemann-Pick Disease
 - Neruonal Ceroid Liopfuscinosis (Batten Disease)
 - Osteopetrosis
 - Pelizaeus-Merzbacher Disease
 - Sandhoff Disease
 - Sanfilippo Syndrome (MPS-III)
 - Scheie Syndrome (MPS-IS)
 - Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
 - Tay-Sachs Disease
 - Wolman Disease
 - X-linked Adrenoleukodystrophy
 


